jscreen and the Mathew Forbes Romer Foundation Expand Multi-Year Partnership to Bring Lifesaving Genetic Testing Resources to South Florida – Florida Hospital News and Healthcare Report
This Tay-Sachs Awareness Month, we reflect on a year of progress, hope, and meaningful change. Together, we’ve advanced research, raised awareness, and supported families facing Tay-Sachs and related genetic diseases of the brain. Read more
September is Tay-Sachs Awareness Month Read More »
Published article in the prestigious Clinical Pharmacology and Therapeutics Journal , titled “Family Driven Development of Treatments for Rare Pediatric Neurological Diseases https://onlinelibrary.wiley.com/share/author/CYASAK6VRRDKH23SJNZB?target=10.1002/cpt.2507
Family Driven Development of Treatments for Rare Pediatric Neurological Diseases Read More »
The Year in Review summary 12/16/21. https://conta.cc/31S4v9J
The Year in Review summary 2021 Read More »
“Sio Gene Therapies Announces Positive Interim Safety and Biomarker Data from Ongoing Phase 1/2 Clinical Study of AXO-AAV-GM1 Gene Therapy in GM1 Gangliosidosis”. https://investors.siogtx.com/news-releases/news-release-details/sio-gene-therapies-announces-positive-interim-safety-and
Sio Gene Therapies Announces First Patient Dosed in Clinical Trial of AXO-AAV-GM2 in Patients with Tay-Sachs and Sandhoff Disease (GM2 Gangliosidosis). Sio https://investors.siogtx.com/news-releases/news-release-details/sio-gene-therapies-announces-first-patient-dosed-clinical-trial?fbclid=IwAR2DaXAujFySSmtAoEIfDF1XhG3Gi56D6CgDkbMD2yWAFQ65kP28GV3G4B0
Taysha Gene Therapies “A Clinical Trial Option for Children with Tay-Sachs Disease or Sandhoff” https://www.tsd-sdgtxtrial.com/?fbclid=IwAR39L0MTuN_B-yXzwFtR-6ifmNtl_evd_CFqduSRfqe4enJckIsCVfG3pFk
AXO-AAV-GM2 is the first investigational gene therapy to receive IND clearance in Tay-Sachs and Sandhoff diseases Represents Axovant’s second IND clearance for a gene therapy program in the last 12 months NEW YORK, Nov. 09, 2020 (GLOBE NEWSWIRE) — Axovant Gene Therapies Ltd. (NASDAQ: AXGT), a clinical-stage company developing innovative gene therapies, today announced that the U.S. Food
TEAM DAD Parenting Series: Dad Highlights Program GAME ON FOR FATHERS OF CHILDREN WITH SPECIAL NEEDS! Join us on November 5th at 7:00pm as we have an in-depth conversation with a father who has taken his experiences as a parent of a child with special needs and created change in his community and in the
TEAM DAD Parenting Series: Dad Highlights Program Read More »
