Published article in the prestigious Clinical Pharmacology and Therapeutics Journal , titled “Family Driven Development of Treatments for Rare Pediatric Neurological Diseases https://onlinelibrary.wiley.com/share/author/CYASAK6VRRDKH23SJNZB?target=10.1002/cpt.2507
The Year in Review summary 12/16/21. https://conta.cc/31S4v9J
“Sio Gene Therapies Announces Positive Interim Safety and Biomarker Data from Ongoing Phase 1/2 Clinical Study of AXO-AAV-GM1 Gene Therapy in GM1 Gangliosidosis”. https://investors.siogtx.com/news-releases/news-release-details/sio-gene-therapies-announces-positive-interim-safety-and
Sio Gene Therapies Announces First Patient Dosed in Clinical Trial of AXO-AAV-GM2 in Patients with Tay-Sachs and Sandhoff Disease (GM2 Gangliosidosis). Sio https://investors.siogtx.com/news-releases/news-release-details/sio-gene-therapies-announces-first-patient-dosed-clinical-trial?fbclid=IwAR2DaXAujFySSmtAoEIfDF1XhG3Gi56D6CgDkbMD2yWAFQ65kP28GV3G4B0
Taysha Gene Therapies “A Clinical Trial Option for Children with Tay-Sachs Disease or Sandhoff” https://www.tsd-sdgtxtrial.com/?fbclid=IwAR39L0MTuN_B-yXzwFtR-6ifmNtl_evd_CFqduSRfqe4enJckIsCVfG3pFk
By Cynthia Stern Schloss When is the big day? Will it be a large wedding? What is your dress like? Where are you going on your honeymoon? Do you plan on starting a family? When are you having genetic testing? Excuse me? Genetic testing is a topic not typically posed to brides-to-be. After all, who …
